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Total database: 17430
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Hasil Pencarian (2)

Avalglucosidase alfa Approved DB16099
biotech | CAS: 1802558-87-7

Avalglucosidase alfa, or NeoGAA, is a drug for enzyme replacement therapy specifically designed for Pompe disease, a rare inherited neuromuscular disorder caused by the deficiency of the alpha-glucosidase (GAA) enzyme. GAA is an essential enzyme that hydrolyz…

Kategori:
Alimentary Tract and MetabolismEnzyme Replacement TherapyEnzymes +2
Target Protein:
Cation-independent mannose-6-phosphate receptor
Waktu ParuhThe mean avalglucos…
Vol. DistribusiThe volume of distr…
KlirensThe mean avalglucos…
Genetik -
Cipaglucosidase alfa Approved DB16708
biotech | CAS: 2359727-71-0

Cipaglucosidase alfa (ATB200) is a novel recombinant human acid alpha-glucosidase (GAA) investigated for the treatment of patients with Pompe disease, a rare inherited metabolic disorder characterized by a deficiency in GAA.[A232955] Other types of enzyme rep…

Kategori:
Alimentary Tract and MetabolismEnzyme Replacement TherapyEnzymes +1
Target Protein:
Cation-independent mannose-6-phosphate receptor
Waktu ParuhThe mean terminal e…
Vol. DistribusiThe mean volume of …
KlirensCoadministration of…
Genetik -