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Risdiplam Approved DB15305
small molecule | CAS: 1825352-65-5

Risdiplam is an orally bioavailable mRNA splicing modifier used for the treatment of spinal muscular atrophy (SMA).[L12615] It increases systemic SMN protein concentrations by improving the efficiency of _SMN2_ gene transcription. This mechanism of action is …

Kategori:
BCRP/ABCG2 SubstratesCytochrome P-450 CYP3A SubstratesCytochrome P-450 CYP3A4 Substrates +11
Waktu ParuhThe terminal elimin…
Vol. DistribusiFollowing oral admi…
KlirensFor a 14.9kg patien…
Genetik -