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Eladocagene exuparvovec Approved DB16780
biotech | CAS: 2098615-91-7

Eladocagene exuparvovec is a recombinant adeno-associated virus-2 (AAV2)-based gene therapy that expresses human aromatic L-amino acid decarboxylase (AADC), and it is used to treat AADC deficiency, a fatal and rare genetic disorder that causes severe disabili…

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Adeno-associated Viral Vector TherapiesAlimentary Tract and MetabolismEnzymes +2
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