Hasil Pencarian (1)
biotech | CAS: 2055732-84-6
Duchenne muscular dystrophy (DMD) is an X-linked recessive allelic disorder characterized by a lack of functional dystrophin protein, which leads to progressive ambulatory, pulmonary, and cardiac function and is invariably fatal. A related, albeit a less seve…
Kategori:
Antisense OligonucleotidesMorpholinesMusculo-Skeletal System
+5
Target Protein:
DMD gene (exon 53 viltolarsen target site)
Waktu ParuhViltolarsen has a r…
Vol. DistribusiViltolarsen has a s…
KlirensViltolarsen has a r…
Genetik
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